Medical management of muscle weakness in Duchenne muscular dystrophy

Author:

Rivera Sarah R.ORCID,Jhamb Sumit K.,Abdel-Hamid Hoda Z.,Acsadi Gyula,Brandsema John,Ciafaloni Emma,Darras Basil T.,Iannaccone Susan T.,Konersman Chamindra G.,Kuntz Nancy L.,McDonald Craig M.,Parsons Julie A.,Tesi Rocha Carolina,Zaidman Craig M.,Butterfield Russell J.ORCID,Connolly Anne M.,Mathews Katherine D.

Publisher

Public Library of Science (PLoS)

Subject

Multidisciplinary

Reference20 articles.

1. Improvement of survival in Duchenne Muscular Dystrophy: retrospective analysis of 835 patients;L Passamano;Acta Myol,2012

2. Long-Term Pulmonary Function in Duchenne Muscular Dystrophy: Comparison of Eteplirsen-Treated Patients to Natural History;TB Kinane;J Neuromuscul Dis,2018

3. Management of Adrenal Insufficiency Risk After Long-term Systemic Glucocorticoid Therapy in Duchenne Muscular Dystrophy: Clinical Practice Recommendations;SA Bowden;J Neuromuscul Dis,2019

4. What Is Duchenne Muscular Dystrophy? duchenneuk 2020 [cited 2020 Feb 4];Available from: URL: https://www.duchenneuk.org/faqs/what-is-duchenne-muscular-dystrophy.

5. Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study;CM McDonald;Lancet,2018

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