Fosmetpantotenate (RE-024), a phosphopantothenate replacement therapy for pantothenate kinase-associated neurodegeneration: Mechanism of action and efficacy in nonclinical models-Reference-Cited by-同舟云学术

Fosmetpantotenate (RE-024), a phosphopantothenate replacement therapy for pantothenate kinase-associated neurodegeneration: Mechanism of action and efficacy in nonclinical models

Published:2018-03-09 Issue:3 Volume:13 Page:e0192028
ISSN:1932-6203
Container-title:PLOS ONE
language:en
Short-container-title:PLoS ONE

Author:

Elbaum Daniel^ORCID,Beconi Maria G.,Monteagudo Edith,Di Marco Annalise,Quinton Maria S.,Lyons Kathryn A.,Vaino Andrew,Harper Steven

Funder

Retrophin Inc. funded the work reported in this manuscript.

Publisher

Public Library of Science (PLoS)

Subject

Multidisciplinary

Reference28 articles.

1. An isoform of hPANK2, deficient in pantothenate kinase-associated neurodegeneration, localizes to mitochondria;K Hortnagel;Hum Mol Genet,2003

2. Pantethine rescues phosphopantothenoylcysteine synthetase and phosphopantothenoylcysteine decarboxylase deficiency in Escherichia coli but not in Pseudomonas aeruginosa;CJ Balibar;J Bacteriol,2011

3. Compartmentalization of mammalian pantothenate kinases;A Alfonso-Pecchio;PLoS One,2012

4. Phenotypes and genotypes of patients with pantothenate kinase-associated neurodegeneration in Asian and Caucasian populations: 2 cases and literature review;CH Lee;Sci World J,2013

5. A novel 3-bp deletion in the PANK2 gene of Dutch patients with pantothenate kinase-associated neurodegeneration: evidence for a founder effect;P Rump;Neurogenetics,2005

Cited by 27 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Metabolomic and proteomic applications to exercise biomedicine;Translational Exercise Biomedicine;2024-03-21

2. Inherited Disorders of Coenzyme A Biosynthesis: Models, Mechanisms, and Treatments;International Journal of Molecular Sciences;2023-03-21

3. Comparative Pharmacology of a Bis-Pivaloyloxymethyl Phosphonate Prodrug Inhibitor of Enolase after Oral and Parenteral Administration;ACS PHARMACOL TRANSL;2023

4. Comparative Pharmacology of a Bis-Pivaloyloxymethyl Phosphonate Prodrug Inhibitor of Enolase after Oral and Parenteral Administration;ACS Pharmacology & Translational Science;2023-01-06

5. Experimental pharmacology: Targeting metabolic pathways;International Review of Neurobiology;2023