Properties of Neurons Derived from Induced Pluripotent Stem Cells of Gaucher Disease Type 2 Patient Fibroblasts: Potential Role in Neuropathology-Reference-Cited by-同舟云学术

Properties of Neurons Derived from Induced Pluripotent Stem Cells of Gaucher Disease Type 2 Patient Fibroblasts: Potential Role in Neuropathology

Published:2015-03-30 Issue:3 Volume:10 Page:e0118771
ISSN:1932-6203
Container-title:PLOS ONE
language:en
Short-container-title:PLoS ONE

Author:

Sun Ying,Florer Jane,Mayhew Christopher N.,Jia Zhanfeng,Zhao Zhiying,Xu Kui,Ran Huimin,Liou Benjamin,Zhang Wujuan,Setchell Kenneth D. R.,Gu Jianguo,Grabowski Gregory A.

Publisher

Public Library of Science (PLoS)

Subject

Multidisciplinary

Reference72 articles.

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4. Improved management of lysosomal glucosylceramide levels in a mouse model of type 1 Gaucher disease using enzyme and substrate reduction therapy;J Marshall;J Inherit Metab Dis,2010

5. Enzyme therapy in type 1 Gaucher disease: comparative efficacy of mannose-terminated glucocerebrosidase from natural and recombinant sources;GA Grabowski;Ann Intern Med,1995

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