The expanded CAG repeat in the huntingtin gene as target for therapeutic RNA modulation throughout the HD mouse brain-Reference-Cited by-同舟云学术

The expanded CAG repeat in the huntingtin gene as target for therapeutic RNA modulation throughout the HD mouse brain

Published:2017-02-09 Issue:2 Volume:12 Page:e0171127
ISSN:1932-6203
Container-title:PLOS ONE
language:en
Short-container-title:PLoS ONE

Author:

Datson Nicole A.,González-Barriga Anchel,Kourkouta Eleni,Weij Rudie,van de Giessen Jeroen,Mulders Susan,Kontkanen Outi,Heikkinen Taneli,Lehtimäki Kimmo,van Deutekom Judith C. T.

Publisher

Public Library of Science (PLoS)

Subject

Multidisciplinary

Reference42 articles.

1. Differential loss of striatal projection neurons in Huntington disease;A Reiner;Proc Natl Acad Sci U S A,1988

2. Evidence for more widespread cerebral pathology in early HD: an MRI-based morphometric analysis;HD Rosas;Neurology,2003

3. A novel gene containing a trinucleotide repeat that is expanded and unstable on Huntington's disease chromosomes;Cell,1993

4. The Biology of Huntingtin;F Saudou;Neuron,2016

5. Mechanisms of RNA-induced toxicity in CAG repeat disorders;R Nalavade;Cell death & disease,2013

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