Potential Risks to Stable Long-term Outcome of Allogeneic Hematopoietic Stem Cell Transplantation for Children With Cerebral X-linked Adrenoleukodystrophy-Reference-Cited by-同舟云学术

Potential Risks to Stable Long-term Outcome of Allogeneic Hematopoietic Stem Cell Transplantation for Children With Cerebral X-linked Adrenoleukodystrophy

Published:2018-07-20 Issue:3 Volume:1 Page:e180769
ISSN:2574-3805
Container-title:JAMA Network Open
language:en
Short-container-title:JAMA Netw Open

Author:

Kühl Jörn-Sven¹,Kupper Jana²,Baqué Hermann³,Ebell Wolfram²,Gärtner Jutta⁴,Korenke Christoph⁵,Spors Birgit⁶,Steffen Ingo G.²,Strauss Gabriele⁷,Voigt Sebastian²,Weschke Bernhard³,Weddige Almuth⁴,Köhler Wolfgang⁸,Steinfeld Robert⁴

Affiliation:

1. Department of Pediatric Hematology/Oncology/Hemostaseology, University Hospital Leipzig, Leipzig, Germany

2. Department of Pediatric Oncology/Hematology/SCT, Charité Campus Virchow-Klinikum, Berlin, Germany

3. Department of Pediatric Neurology, Charité Campus Virchow-Klinikum, Berlin, Germany

4. Department of Pediatric Neurology, University Medical Center Göttingen, Göttingen, Germany

5. Department of Pediatric Neurology, Klinikum Oldenburg, Oldenburg, Germany

6. Department of Pediatric Radiology, Charité Campus Virchow-Klinikum, Berlin, Germany

7. Department of Pediatrics, Helios-Klinikum Berlin-Buch, Berlin, Germany

8. Department of Neurology, University Hospital Leipzig, Leipzig, Germany

Publisher

American Medical Association (AMA)

Subject

General Medicine

Link

http:///jamanetworkopen/article-pdf/1/3/e180769/17326180/khl_2018_oi_180058.pdf

Reference31 articles.

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2. X-linked adrenoleukodystrophy (X-ALD): clinical presentation and guidelines for diagnosis, follow-up and management.;Engelen;Orphanet J Rare Dis,2012

3. The genetic landscape of X-linked adrenoleukodystrophy: inheritance, mutations, modifier genes, and diagnosis.;Wiesinger;Appl Clin Genet,2015

4. Therapeutic strategies in adrenoleukodystrophy.;Turk;Wien Med Wochenschr,2017

5. Cerebral X-linked adrenoleukodystrophy: the international hematopoietic cell transplantation experience from 1982 to 1999.;Peters;Blood,2004

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