1. John Walton Muscular Dystrophy Research Centre, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, England
2. Department of Neurology, University of Rochester Medical Center, Rochester, New York
3. Department of Biostatistics and Computational Biology, University of Rochester Medical Center, Rochester, New York
4. Newcastle University, Newcastle upon Tyne, England
5. NIHR Clinical Research Network North East and North Cumbria, Newcastle upon Tyne, England
6. Department of Neuropediatrics and Muscle Disorders, Faculty of Medicine, University Hospital Freiburg, Freiburg, Germany
7. Department of Neuropediatrics, University Hospital Bonn, Bonn, Germany
8. Ohio State University, Columbus
9. Robert Jones and Agnes Hunt Orthopaedic Hospital, NHS Foundation Trust, Oswestry, England
10. Leeds General Infirmary, Leeds, England
11. David Geffen School of Medicine, University of California, Los Angeles
12. Alderhey Children’s Hospital NHS Foundation Trust, Liverpool, England
13. Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan, Italy
14. Dubowitz Neuromuscular Centre, UCL NIHR GOSH Biomedical Research Centre, UCL Great Ormond Street Institute of Child Health, London, England
15. Department of Pediatric Neurology, University of Utah, Salt Lake City
16. Glasgow Paediatric Neuromuscular Research Centre, Greater Glasgow and Clyde NHS Yorkhill Hospital, Glasgow, Scotland
17. University Hospitals Birmingham NHS Foundation Trust, Birmingham, England
18. Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children’s Hospital, Columbus, Ohio
19. Ann & Robert H. Lurie Children’s Hospital of Chicago, Chicago, Illinois
20. Great Ormond Street Hospital, London, England
21. Department of Neurology, Boston Children’s Hospital and Harvard Medical School, Boston, Massachusetts
22. Paul and Sheila Wellstone Muscular Dystrophy Center and Department of Neurology, University of Minnesota Medical School, Minneapolis
23. Health Sciences Center, University of New Mexico, Albuquerque
24. Cumming School of Medicine, University of Calgary and Alberta Children’s Hospital Research Institute, Calgary, Canada
25. Neuromuscular Center, AOU Città della Salute e della Scienza, University of Turin, Turin, Italy
26. Abteilung Neuropädiatrie, Medizinische Fakultät Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany
27. Nemours Children’s Hospital, Orlando, Florida
28. Center for Experimental Neurotherapeutics, St Jude Children’s Research Hospital, Memphis, Tennessee
29. Penn State Health Milton S. Hershey Medical Center, Hershey, Pennsylvania
30. Department of Neurology, School of Medicine, University of Colorado, Aurora
31. Department of Physical Medicine and Rehabilitation and Department of Pediatrics, University of California–Davis, Sacramento
32. Clinic for Pediatrics I, Pediatric Neurology, University Hospital Essen, Essen, Germany
33. Department of Pediatrics and Adolescent Medicine, Division of Pediatric Neurology, University Medical Center Göttingen, Göttingen, Germany
34. University of Missouri, Columbia
35. University of Kansas Medical Center, Kansas City
36. Departments of Pediatrics, Clinical Neurological Sciences, and Epidemiology, University of Western Ontario, London, Canada
37. ERN Neuromuscular Unit, Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy
38. Unit of Neurology, IRCCS Centro Neurolesi Bonino-Pulejo, Messina, Italy
39. School of Medicine, University of North Carolina, Chapel Hill
40. Royal Manchester Children’s Hospital, Manchester, England
41. Children’s Hospital of Eastern Ontario Research Institute, University of Ottawa, Ottawa, Canada
42. ERN Neuromuscular Unit, Department of Neuroscience, University of Padova, Padua, Italy
43. Vanderbilt University Medical Center, Nashville, Tennessee
44. Department of Neurology, Virginia Commonwealth University, Richmond
45. Children’s National Hospital, George Washington University, Washington, DC