Effect of Poloxamer 188 vs Placebo on Painful Vaso-Occlusive Episodes in Children and Adults With Sickle Cell Disease

Author:

Casella James F.1,Barton Bruce A.2,Kanter Julie34,Black L. Vandy56,Majumdar Suvankar78,Inati Adlette910,Wali Yasser11,Drachtman Richard A.12,Abboud Miguel R.13,Kilinc Yurdanur14,Fuh Beng R.15,Al-Khabori Murtadha K.11,Takemoto Clifford M.116,Salman Emad17,Sarnaik Sharada A.1819,Shah Nirmish20,Morris Claudia R.2122,Keates-Baleeiro Jennifer23,Raj Ashok24,Alvarez Ofelia A.25,Hsu Lewis L.26,Thompson Alexis A.27,Sisler India Y.28,Pace Betty S.29,Noronha Suzie A.30,Lasky Joseph L.3132,de Julian Elena Cela33,Godder Kamar34,Thornburg Courtney Dawn3536,Kamberos Natalie L.3738,Nuss Rachelle39,Marsh Anne M.4041,Owen William C.42,Schaefer Anne43,Tebbi Cameron K.44,Chantrain Christophe F.45,Cohen Debra E.4647,Karakas Zeynep48,Piccone Connie M.4950,George Alex5152,Fixler Jason M.53,Singleton Tammuella C.5455,Moulton Thomas5657,Quinn Charles T.58,de Castro Lobo Clarisse Lopes59,Almomen Abdulkareem M.60,Goyal-Khemka Meenakshi6162,Maes Philip63,Emanuele Marty6465,Gorney Rebecca T.1,Padgett Claire S.6566,Parsley Ed6567,Kronsberg Shari S.2,Kato Gregory J.6869,Gladwin Mark T.69

Affiliation:

1. Johns Hopkins University School of Medicine, Baltimore, Maryland

2. University of Massachusetts Medical School, Worcester

3. Medical University of South Carolina, Charleston

4. University of Alabama at Birmingham, Birmingham

5. Our Lady of the Lake Regional Medical Center, Baton Rouge, Louisiana

6. University of Florida College of Medicine, Gainesville

7. University of Mississippi Medical Center, Jackson

8. Children’s National Hospital, Washington, DC

9. Lebanese American University, Byblos and Beirut, Lebanon

10. Nini Hospital, Tripoli, Lebanon

11. Sultan Qaboos University, Muscat, Oman

12. Rutgers University, New Brunswick, New Jersey

13. American University of Beirut Medical Center, Beirut, Lebanon

14. Çukurova University Medical Faculty Balcali Hospital, University of Çukurova, Adana, Turkey

15. East Carolina University, Greenville, North Carolina

16. St Jude Children’s Research Hospital, Memphis, Tennessee

17. Golisano Children’s Hospital of Southwest Florida, Ft Myers

18. Wayne State University School of Medicine, Detroit, Michigan

19. Children’s Hospital of Michigan, Detroit

20. Duke University School of Medicine, Durham, North Carolina

21. Emory University School of Medicine, Atlanta, Georgia

22. Children’s Healthcare of Atlanta, Atlanta, Georgia

23. T.C. Thompson Children’s Hospital at Erlanger, University of Tennessee, Chattanooga

24. University of Louisville/Norton Children’s Hospital, Louisville, Kentucky

25. University of Miami, Miami, Florida

26. University of Illinois at Chicago, Chicago

27. Ann & Robert H. Lurie Children’s Hospital of Chicago, Feinberg School of Medicine, Northwestern University, Evanston, Illinois

28. Children’s Hospital of Richmond at Virginia Commonwealth University, Richmond

29. Augusta University, Augusta, Georgia

30. University of Rochester School of Medicine and Dentistry, Golisano Children’s Hospital at University of Rochester Medical Center, Rochester, New York

31. Harbor-UCLA Medical Center, Torrance, California

32. Cure 4 The Kids Foundation, Las Vegas, Nevada

33. Hospital General Universitario Gregorio Marañón, Universidad Complutense de Madrid, Madrid, Spain

34. Nicklaus Children’s Hospital, Miami, Florida

35. Rady Children’s Hospital - San Diego, San Diego, California

36. UC San Diego School of Medicine, La Jolla, California

37. University of Iowa Children’s Hospital, Iowa City

38. Loyola University Medical Center, Maywood, Illinois

39. Children’s Hospital Colorado, University of Colorado, Aurora

40. UCSF Benioff Children’s Hospital Oakland (UBCHO), Oakland, California

41. University of Wisconsin–Madison, Madison

42. Children’s Hospital of the King’s Daughters, Norfolk, Virginia

43. Joe DiMaggio Children’s Hospital, Hollywood, Florida

44. Tampa General Hospital, Tampa, Florida

45. Clinique MontLegia, CHC, Liège, Belgium

46. UPMC Children’s Hospital of Pittsburgh, Pittsburgh, Pennsylvania

47. Studer Family Children’s Hospital Ascension Sacred Heart, University of Florida, Pensacola

48. Istanbul Faculty of Medicine, Istanbul University, Istanbul, Turkey

49. Rainbow Babies and Children’s Hospital, Cleveland, Ohio

50. Carle Foundation Hospital, Urbana, Illinois

51. Baylor College of Medicine, Houston, Texas

52. Wake Forest School of Medicine, Winston-Salem, North Carolina

53. The Herman and Walter Samuelson Children’s Hospital at Sinai, Baltimore, Maryland

54. Tulane University, New Orleans, Louisiana

55. Mississippi Center for Advanced Medicine, Slidell, Louisiana

56. Bronx-Lebanon Hospital, Bronx, New York City, New York

57. Bayer Pharmaceuticals, Whippany, New Jersey

58. Cincinnati Children’s Hospital Medical Center, Cincinnati, Ohio

59. Instituto estadual de Hematologia Arthur de Siqueira Cavalcanti – HEMORIO, Rio de Janeiro, Brasil

60. Blood and Cancer Center, King Khalid University Hospital (KKUH), King Saud University Medical City, Riyadh, Saudi Arabia

61. Phoenix Children’s Hospital, Phoenix, Arizona

62. Rutgers Cancer Institute of New Jersey, New Brunswick

63. University Hospital of Antwerp (UZA), Edegem, Belgium

64. Visgenx, San Diego, California

65. Mast Therapeutics Inc, San Diego, California

66. Sanifit Therapeutics, San Diego, California

67. Biotechnology, San Diego, California

68. CSL Behring, King of Prussia, Pennsylvania

69. University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania

Publisher

American Medical Association (AMA)

Subject

General Medicine

Reference18 articles.

1. Pharmacological interventions for painful sickle cell vaso-occlusive crises in adults.;Cooper;Cochrane Database Syst Rev,2019

2. Mortality in sickle cell disease: life expectancy and risk factors for early death.;Platt;N Engl J Med,1994

3. Hospital readmission for adult acute sickle cell painful episodes: frequency, etiology, and prognostic significance.;Ballas;Am J Hematol,2005

4. Pathophysiology of sickle cell disease.;Sundd;Annu Rev Pathol,2019

5. Sickle cell disease.;Piel;N Engl J Med,2017

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