Outcome Measures for Clinical Trials of Leber Congenital Amaurosis Caused by the Intronic Mutation in the CEP290 Gene-Reference-Cited by-同舟云学术

Outcome Measures for Clinical Trials of Leber Congenital Amaurosis Caused by the Intronic Mutation in the CEP290 Gene

Published:2017-05-16 Issue:5 Volume:58 Page:2609
ISSN:1552-5783
Container-title:Investigative Opthalmology & Visual Science
language:en
Short-container-title:Invest. Ophthalmol. Vis. Sci.

Author:

Jacobson Samuel G.¹,Cideciyan Artur V.¹,Sumaroka Alexander¹,Roman Alejandro J.¹,Charng Jason¹,Lu Monica¹,Choi Windy¹,Sheplock Rebecca¹,Swider Malgorzata¹,Kosyk Mychajlo S.¹,Schwartz Sharon B.¹,Stone Edwin M.²,Fishman Gerald A.³

Affiliation:

1. Scheie Eye Institute, Department of Ophthalmology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, Pennsylvania, United States

2. Department of Ophthalmology and Visual Science, Carver College of Medicine, Stephen A. Wynn Institute for Vision Research, University of Iowa, Iowa City, Iowa, United States

3. Pangere Center for Hereditary Retinal Diseases, The Chicago Lighthouse, Chicago, Illinois, United States

Publisher

Association for Research in Vision and Ophthalmology (ARVO)

Subject

General Medicine

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