Stem cell-derived neurotrophic support for the neuromuscular junction in spinal muscular atrophy
Author:
Publisher
Informa Healthcare
Subject
Clinical Biochemistry,Drug Discovery,Pharmacology
Link
http://www.tandfonline.com/doi/pdf/10.1517/14712598.2010.529895
Reference73 articles.
1. Quantitative Analyses of SMN1 and SMN2 Based on Real-Time LightCycler PCR: Fast and Highly Reliable Carrier Testing and Prediction of Severity of Spinal Muscular Atrophy
2. Alternative Splicing Events Are a Late Feature of Pathology in a Mouse Model of Spinal Muscular Atrophy
3. Identification and characterization of a spinal muscular atrophy-determining gene
4. Spinal muscular atrophy: mechanisms and therapeutic strategies
5. Reduced SMN protein impairs maturation of the neuromuscular junctions in mouse models of spinal muscular atrophy
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