Gene therapy of metachromatic leukodystrophy
Author:
Publisher
Informa Healthcare
Subject
Clinical Biochemistry,Drug Discovery,Pharmacology
Link
http://www.tandfonline.com/doi/pdf/10.1517/14712598.5.1.55
Reference47 articles.
1. THE INCIDENCE AND GENETICS OF METACHROMATIC LEUCODYSTROPHY IN NORTHERN SWEDEN
2. Leukodystrophy incidence in Germany
3. A Myelin Galactolipid, Sulfatide, Is Essential for Maintenance of Ion Channels on Myelinated Axon But Not Essential for Initial Cluster Formation
4. Sulfatide is a negative regulator of oligodendrocyte differentiation: Development in sulfatide-null mice
5. Phenotype of arylsulfatase A-deficient mice: Relationship to human metachromatic leukodystrophy
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