Enzyme replacement therapy for Fabry disease: lessons from two α-galactosidase A orphan products and one FDA approval
Author:
Publisher
Informa Healthcare
Subject
Clinical Biochemistry,Drug Discovery,Pharmacology
Link
http://www.tandfonline.com/doi/pdf/10.1517/14712598.4.7.1167
Reference27 articles.
1. A biochemical and pharmacological comparison of enzyme replacement therapies for the glycolipid storage disorder Fabry disease
2. Comparative evaluation of α-galactosidase A infusions for treatment of Fabry disease
3. Prevalence of Lysosomal Storage Disorders
4. Novel Frameshift Mutation in a Heterozygous Woman with Fabry Disease and End-Stage Renal Failure
5. Anderson-Fabry disease: clinical manifestations and impact of disease in a cohort of 60 obligate carrier females
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