Gene therapy for leukodystrophy: progress, challenges and opportunities
Author:
Funder
INSERM and University Paris-Sud
Publisher
Informa Healthcare
Subject
Pharmacology (medical),Health Policy,Pharmacology, Toxicology and Pharmaceutics (miscellaneous)
Link
http://www.tandfonline.com/doi/pdf/10.1517/21678707.2016.1151352
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1. Gene therapy returns to centre stage
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5. Leukoencephalopathy With Vanishing White Matter: A Review
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