An overview of health technology assessments of gene therapies with the focus on cost-effectiveness models-Reference-Cited by-同舟云学术

An overview of health technology assessments of gene therapies with the focus on cost-effectiveness models

Published:2021-01-01 Issue:1 Volume:9 Page:
ISSN:2001-6689
Container-title:Journal of Market Access & Health Policy
language:en
Short-container-title:Journal of Market Access & Health Policy

Author:

Pochopień Michał¹²,Paterak Ewelina²,Clay Emilie³,Janik Justyna²,Aballea Samuel¹⁴,Biernikiewicz Małgorzata⁵,Toumi Mondher¹⁶

Affiliation:

1. Public Health Department, University of Aix-Marseille, Marseille, France

2. Modelling, Creativ-Ceutical, Kraków, Poland

3. Modelling, Creativ-Ceutical, Paris, France

4. HEOR, Creativ-Ceutical, Rotterdam, Netherlands

5. Medical Writing and Publishing, Creativ-Ceutical, Kraków, Poland

6. HEOR, Creativ-Ceutical, Paris, France

Funder

no funding

Publisher

Informa UK Limited

Link

https://www.tandfonline.com/doi/pdf/10.1080/20016689.2021.2002006

Reference27 articles.

1. Marsden G, Towse A, Pearson SD, et al. Gene therapy: understanding the science, assessing the evidence, and paying for value. ICER; 2017. Available from: https://www.ohe.org/publications/gene-therapy-understanding-science-assessing-evidence-and-paying-value

2. ICER. Spinraza® and Zolgensma® for Spinal Muscular Atrophy: effectiveness and Value. Final Evidence Report; 2019. Available from: https://icer-review.org/material/sma-final-evidence-report/

3. NICE. Talimogene laherparepvec for treating unresectable metastatic melanoma. Technology appraisal guidance [TA410]; 2016. Available from: https://www.nice.org.uk/guidance/ta410

4. NICE. Strimvelis for treating adenosine deaminase deficiency–severe combined immunodeficiency.Highly specialised technologies guidance [HST7]; 2018. [cited 2020 Oct 20]. Available from: https://www.nice.org.uk/guidance/hst7

5. CADTH. Tisagenlecleucel (Kymriah) for Pediatric Acute Lymphoblastic Leukemia and Diffuse Large B-Cell Lymphoma; 2019. Available from: https://www.cadth.ca/tisagenlecleucel-kymriah-pediatric-acute-lymphoblastic-leukemia-and-diffuse-large-b-cell-lymphoma

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