Health economic evaluation of gene replacement therapies: methodological issues and recommendations-Reference-Cited by-同舟云学术

Health economic evaluation of gene replacement therapies: methodological issues and recommendations

Published:2020-01-01 Issue:1 Volume:8 Page:1822666
ISSN:2001-6689
Container-title:Journal of Market Access & Health Policy
language:en
Short-container-title:Journal of Market Access & Health Policy

Author:

Aballéa Samuel¹,Thokagevistk Katia²,Velikanova Rimma³,Simoens Steven⁴,Annemans Lieven⁵,Antonanzas Fernando⁶,Auquier Pascal⁷,François Clément²⁸,Fricke Frank-Ulrich⁹,Malone Daniel¹⁰,Millier Aurélie²,Persson Ulf¹¹,Petrou Stavros¹²,Dabbous Omar¹³,Postma Maarten³^ORCID,Toumi Mondher²⁸^ORCID

Affiliation:

1. Creativ-Ceutical, HEOR, Rotterdam, Netherlands

2. Creativ-Ceutical, HEOR, Paris, France

3. Groningen Research Institute of Pharmacy, PharmacoTherapy, Epidemiology & Economics, University of Groningen, Groningen, Netherlands

4. Department of Pharmaceutical and Pharmacological Sciences, KU Leuven, Leuven, Belgium

5. Department of Public Health, Ghent University, Ghent, Belgium

6. Department of Economics, University of La Rioja, Logroño, Spain

7. CEReSS - Health Service Research and Quality of Life Center, Aix-Marseille University, Marseille, France

8. Public Health Department - Research Unit, Aix-Marseille University, Marseille, France

9. Technische Hochschule Nürnberg, Nürnberg, Germany

10. Pharmacotherapy Faculty, College of Pharmacy, University of Utah, Salt Lake City, USA

11. The Swedish Institute for Health Economics (IHE), Lund, Sweden

12. Nuffield Department of Primary Care Health Sciences, University of Oxford, Oxford, UK

13. Global Health Economics and Outcomes Research and Real World EvidenceAveXis Inc, Novartis Gene Therapies, Bannockburn, IL, USA

Funder

Novartis Gene Therapies

Publisher

Informa UK Limited

Link

https://www.tandfonline.com/doi/pdf/10.1080/20016689.2020.1822666

Reference99 articles.

1. Drug discovery and development for rare genetic disorders

2. Gene Therapy and Genome Editing

3. Replacement Therapies in Metabolic Disease

4. Gene therapy: evidence, value and affordability in the US health care system

5. Gene therapy comes of age

Cited by 22 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Market Access Challenges and Solutions in Cell and Gene Therapy in The Netherlands;Journal of Market Access & Health Policy;2024-07-30

2. Advanced therapeutic approaches in sarcoglycanopathies;Current Opinion in Pharmacology;2024-06

3. A Review of the Cost-Effectiveness Evidence for FDA-Approved Cell and Gene Therapies;Human Gene Therapy;2024-06-01

4. Using automated text classification to explore uncertainty in NICE appraisals for drugs for rare diseases;International Journal of Technology Assessment in Health Care;2024

5. A systematic review on the appropriate discounting rates for the economic evaluation of gene therapies: whether a specific approach is justified to tackle the challenges?;International Journal of Technology Assessment in Health Care;2024