AAV gene delivery to the spinal cord: serotypes, methods, candidate diseases, and clinical trials
Author:
Affiliation:
1. Department of Neurosurgery, Emory University, Atlanta, GA, USA
Publisher
Informa UK Limited
Subject
Clinical Biochemistry,Drug Discovery,Pharmacology
Link
https://www.tandfonline.com/doi/pdf/10.1080/14712598.2018.1416089
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1. Gene Therapy of Canavan Disease: AAV-2 Vector for Neurosurgical Delivery of Aspartoacylase Gene (ASPA) to the Human Brain
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4. Intraspinal cord delivery of IGF-I mediated by adeno-associated virus 2 is neuroprotective in a rat model of familial ALS
5. Adeno-Associated Virus (AAV) Vectors in the CNS
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