Developments in reading frame restoring therapy approaches for Duchenne muscular dystrophy
Author:
Affiliation:
1. Department of Human Genetics, Leiden University Medical Center, Leiden, The Netherlands
Funder
Duchenne Parent Project
Publisher
Informa UK Limited
Subject
Clinical Biochemistry,Drug Discovery,Pharmacology
Link
https://www.tandfonline.com/doi/pdf/10.1080/14712598.2021.1832462
Reference129 articles.
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4. Diagnosis and management of Duchenne muscular dystrophy, part 3: primary care, emergency management, psychosocial care, and transitions of care across the lifespan
5. Dystrophin: The protein product of the duchenne muscular dystrophy locus
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