Real world data for rare diseases research: The beginner’s guide to registries-Reference-Cited by-同舟云学术

Real world data for rare diseases research: The beginner’s guide to registries

Published:2023-08 Issue:1 Volume:11 Page:9-15
ISSN:2167-8707
Container-title:Expert Opinion on Orphan Drugs
language:en
Short-container-title:Expert Opinion on Orphan Drugs

Author:

Pisa Federica¹,Arias Ariel²,Bratton Emily³⁴,Salas Maribel⁵,Sultana Janet⁶

Affiliation:

1. Bayer AG, Berlin, Germany

2. Faculty of Pharmacy, Université de Montreal, Montreal, QC, Canada

3. IQVIA, Durham, NC, USA

4. University of North Carolina, Chapel Hill, USA

5. Daiichi Sankyo Inc and University of Pennsylvania, Bernards, NJ, USA

6. Exeter College of Medicine and Health, University of Exeter, Exeter, UK

Publisher

Informa UK Limited

Subject

Pharmacology (medical),Health Policy,Pharmacology, Toxicology and Pharmaceutics (miscellaneous)

Link

https://www.tandfonline.com/doi/pdf/10.1080/21678707.2023.2241347

Reference45 articles.

1. Food and Drug Administration. Framework for FDA’s real-world evidence program. U.S. Food And Drug Administration Dec 2018. [cited 2022 Dec 20]; Available from: https://www.fda.gov/media/120060/download.

2. The European Network for Centres for Pharmacoepidemiology and Pharmacovigilance (ENCePP). Guide on methodological standards in pharmacoepidemiology. [cited 2022 Dec 19]; Available from: https://www.encepp.eu/standards_and_guidances/methodologicalGuide15_6.shtml.

3. Real‐World Data for Regulatory Decision Making: Challenges and Possible Solutions for Europe

4. A review of uses of health care utilization databases for epidemiologic research on therapeutics

5. Role of Epidemiological Data Within the Drug Development Lifecycle: A Chronic Migraine Case Study

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