A Phase 2, Double-Blind, Randomized, Dose-Ranging Trial Of Reldesemtiv In Patients With ALS

Author:

Shefner Jeremy M.1,Andrews Jinsy A.2,Genge Angela3,Jackson Carlayne4,Lechtzin Noah5,Miller Timothy M.6,Cockroft Bettina M.7,Meng Lisa7,Wei Jenny7,Wolff Andrew A.7,Malik Fady I.7,Bodkin Cynthia8,Brooks Benjamin R.9,Caress James10,Dionne Annie11,Fee Dominic12,Goutman Stephen A.13,Goyal Namita A.14,Hardiman Orla15,Hayat Ghazala16,Heiman-Patterson Terry17,Heitzman Daragh18,Henderson Robert D.19,Johnston Wendy20,Karam Chafic21,Kiernan Matthew C.22,Kolb Stephen J.23,Korngut Lawrence24,Ladha Shafeeq25,Matte Genevieve26,Mora Jesus S.27,Needham Merrilee28,Oskarsson Bjorn29ORCID,Pattee Gary L.30,Pioro Erik P.31,Pulley Michael32,Quan Dianna33,Rezania Kourosh34,Schellenberg Kerri L.35ORCID,Schultz David36,Shoesmith Christen37,Simmons Zachary38,Statland Jeffrey39,Sultan Shumaila40,Swenson Andrea41,Berg Leonard H. Van Den42,Vu Tuan43,Vucic Steve44,Weiss Michael45,Whyte-Rayson Ashley46,Wymer James47,Zinman Lorne48,Rudnicki Stacy A.7

Affiliation:

1. Barrow Neurological Institute, Phoenix, AZ, USA

2. The Eleanor and Lou Gehrig ALS Center, The Neurological Institute, New York, NY, USA

3. Montreal Neurological Institute, Montreal, QC, Canada

4. University of Texas Health Science Center, San Antonio, TX, USA

5. Johns Hopkins School of Medicine, Baltimore, MD, USA

6. Washington University School of Medicine, St. Louis, MO, USA

7. Cytokinetics, Inc, South San Francisco, CA, USA

8. Indiana University School of Medicine, Indianapolis, IN, USA

9. Atrium Health Neurosciences Institute–Carolinas Neuromuscular/ALS MDA Care Center, Charlotte, NC, USA

10. Wake Forest Health Sciences, Winston-Salem, NC, USA

11. CHU de Québec, Université Laval, Quebec, Canada

12. Medical College of Wisconsin, Milwaukee, WI, USA

13. University of Michigan, Ann Arbor, MI, USA

14. The ALS & Neuromuscular Center, UCI Health, Orange, CA, USA

15. Trinity College, Beaumont Hospital, Dublin, Ireland

16. St. Louis University, St. Louis, MO, USA

17. Lewis Katz School of Medicine, Temple University, Philadelphia, PA, USA

18. Texas Neurology, Dallas, TX, USA

19. Royal Brisbane and Women's Hospital, Herston, Australia

20. University of Alberta, Edmonton, AB, Canada

21. Oregon Health & Science University, Portland, OR, USA

22. Royal Prince Alfred Hospital, University of Sydney, Sydney, Australia

23. Wexner Medical Center, Ohio State University, Columbus, OH, USA

24. University of Calgary, Calgary, AB, Canada

25. St. Joseph's Hospital and Medical Center, Neurological Institute, AZ, USA Barrow Phoenix

26. Centre Hospitalier de l’Université de Montréal, Montreal, QC, Canada

27. Hospital San Rafael, Madrid, Germany

28. Perron Institute, Department of Neurology, Fiona Stanley Hospital, The University of Notre Dame Australia, Murdoch University, Perth, Australia

29. Mayo Clinic Florida, Jacksonville, FL, USA

30. Neurology Associates, Lincoln, NE, USA

31. Cleveland Clinic, Cleveland, OH, USA

32. University of Florida, Jacksonville, FL, USA

33. University of Colorado Denver, Aurora, CO, USA

34. University of Chicago Medical Center, Chicago, IL, USA

35. University of Saskatchewan, Saskatoon, SK, Canada

36. Flinders Medical Centre, Bedford Park, Australia

37. London Health Sciences Centre, London, ON, Canada

38. Penn State Hershey Medical Center, Hershey, PA, USA

39. University of Kansas Medical Center, Kansas City, KS, USA

40. West Virginia University, Morgantown, WV, USA

41. University of Iowa, Iowa City, IA, USA

42. Department of Neurology, UMC Utrecht Brain Center, University Medical Center Utrecht, Utrecht, The Netherlands

43. University of South Florida, Tampa, FL, USA

44. Westmead Hospital, Sydney, Australia

45. University of Washington, Seattle, WA, USA

46. Duke University School of Medicine, Durham, NC, USA

47. University of Florida, Gainesville, FL, USA

48. ALS/Neuromuscular Clinic Sunnybrook Health Sciences Centre, University of Toronto, Toronto, ON, Canada

Funder

Cytokinetics, Inc.

South San Francisco, CA, USA

Astellas Pharma Inc.

Cytokinetics

Astellas. Cytokinetics, Inc.

Kakuri Omari, PhD, CMPP

Evidence Scientific Solutions, Inc.

Publisher

Informa UK Limited

Subject

Clinical Neurology,Neurology

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