1. Division of Hematology, Division of Pediatric Hematology/Oncology, Duke University School of Medicine, Durham, North Carolina, USA
2. Department of Internal Medicine, VCU Health, Richmond, Virginia, USA
3. Division of Pediatric Hematology/Oncology, University of Miami, Miami, Florida, USA
4. Policy Analysis Inc. (PAI), Brookline, Massachusetts, USA
5. Global Blood Therapeutics, South San Francisco, California, USA