Production of Therapeutic Enzymes by Lentivirus Transgenesis

Author:

Rodríguez María Celeste,Ceaglio Natalia,Antuña Sebastián,Tardivo María Belén,Etcheverrigaray Marina,Prieto Claudio

Publisher

Springer Singapore

Reference78 articles.

1. Bandaranayake AD, Almo SC (2014) Recent advances in mammalian protein production. FEBS Lett 588(2):253–260

2. Baranyi L, Roy A, Embree HD, Dropulic B (2010) Lentiviral vector-mediated genetic modification of cell substrates for the manufacture of proteins and other biologics. PDA J Pharm Sci Technol 64:379–385

3. Bennett LL, Mohan D (2013) Gaucher disease and its treatment options. Ann Pharmacother 47(9):1182–93

4. Braulke T, Bonifacino JS (2009) Sorting of lysosomal proteins. BBA – Mol Cell Res 1793:605–614

5. Braunlin E, Rosenfeld H, Kampmann C et al (2013) Enzyme replacement therapy for mucopolysaccharidosis VI: long-term cardiac effects of galsulfase (Naglazyme®) therapy. J Inherit Metab Dis 36(2):385–394

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