Novel RNA-targeted therapies for hereditary ATTR amyloidosis and their impact on the autonomic nervous system
Author:
Publisher
Springer Science and Business Media LLC
Subject
Neurology (clinical),Endocrine and Autonomic Systems
Link
http://link.springer.com/content/pdf/10.1007/s10286-019-00626-8.pdf
Reference31 articles.
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3. Gertz MA (2017) Hereditary ATTR amyloidosis: burden of illness and diagnostic challenges. Am J Manag Care 23(7 Suppl):S107–S112
4. Conceição I, González-Duarte A, Obici L, Schmidt HH, Simoneau D, Ong ML, Amass L (2016) “Red-flag” symptom clusters in transthyretin familial amyloid polyneuropathy. J Peripher Nerv Syst 21(1):5–9. https://doi.org/10.1111/jns.12153
5. Suhr OB, Lundgren E, Westermark P (2017) One mutation, two distinct disease variants: unravelling the impact of transthyretin amyloid fibril composition. J Intern Med 281:337–347
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