Onasemnogene Abeparvovec: First Global Approval-Reference-Cited by-同舟云学术

Onasemnogene Abeparvovec: First Global Approval

Published:2019-07 Issue:11 Volume:79 Page:1255-1262
ISSN:0012-6667
Container-title:Drugs
language:en
Short-container-title:Drugs

Author:

Hoy Sheridan M.

Publisher

Springer Science and Business Media LLC

Subject

Pharmacology (medical)

Link

http://link.springer.com/content/pdf/10.1007/s40265-019-01162-5.pdf

Reference32 articles.

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3. Verhaart IEC, Robertson A, Wilson IJ, et al. Prevalence, incidence and carrier frequency of 5q-linked spinal muscular atrophy: a literature review. Orphanet J Rare Dis. 2017;12(1):124.

4. Shorrock HK, Gillingwater TH, Groen EJN. Overview of current drugs and molecules in development for spinal muscular atrophy therapy. Drugs. 2018;78(3):293–305.

5. Feldkötter M, Schwarzer V, Wirth R, et al. Quantitative analyses of SMN1 and SMN2 based on real-time lightCycler PCR: fast and highly reliable carrier testing and prediction of severity of spinal muscular atrophy. Am J Hum Genet. 2002;70(2):358–68.

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