Clinical management of Duchenne muscular dystrophy: the state of the art
Author:
Publisher
Springer Science and Business Media LLC
Subject
Psychiatry and Mental health,Clinical Neurology,Dermatology,General Medicine
Link
http://link.springer.com/article/10.1007/s10072-018-3555-3/fulltext.html
Reference68 articles.
1. Ryder S, Leadley RM, Armstrong N, Westwood M, de Kock S, Butt T, Jain M, Kleijnen J (2017) The burden, epidemiology, costs and treatment for Duchenne muscular dystrophy: an evidence review. Orphanet J Rare Dis 12(1):79. https://doi.org/10.1186/s13023-017-0631-3
2. Chamberlain JR, Chamberlain JS (2017) Progress toward gene therapy for Duchenne muscular dystrophy. Mol Ther 25(5):1125–1131. https://doi.org/10.1016/j.ymthe.2017.02.019
3. Niks EH, Aartsma-Rus A (2017) Exon skipping: a first in class strategy for Duchenne muscular dystrophy. Expert Opin Biol Ther 17(2):225–236. https://doi.org/10.1080/14712598.2017.1271872
4. Guiraud S, Chen H, Burns DT, Davies KE (2015) Advances in genetic therapeutic strategies for Duchenne muscular dystrophy. Exp Physiol 100(12):1458–1467. https://doi.org/10.1113/EP085308
5. Van Ruiten H, Bushby K, Guglieri M (2017) State-of-the-art advances in Duchenne muscular dystrophy. EMJ 2(1):90–99
Cited by 27 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. How Can Proteomics Help to Elucidate the Pathophysiological Crosstalk in Muscular Dystrophy and Associated Multi-System Dysfunction?;Proteomes;2024-01-16
2. Real-world evidence of eteplirsen treatment effects in patients with Duchenne muscular dystrophy in the USA;Journal of Comparative Effectiveness Research;2023-09
3. Extracellular Matrix Proteomics: The mdx-4cv Mouse Diaphragm as a Surrogate for Studying Myofibrosis in Dystrophinopathy;Biomolecules;2023-07-12
4. Social cognition in DMD and BMD dystrophinopathies: A cross-sectional preliminary study;The Clinical Neuropsychologist;2023-04-20
5. Analysis of Long Noncoding RNAs-Related Regulatory Mechanisms in Duchenne Muscular Dystrophy Using a Disease-Related lncRNA-mRNA Pathway Network;Genetics Research;2022-12-14
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3