Nusinersen in adults with type 3 spinal muscular atrophy: long-term outcomes on motor and respiratory function
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Springer Science and Business Media LLC
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https://link.springer.com/content/pdf/10.1007/s10072-024-07515-7.pdf
Reference10 articles.
1. Mercuri E et al (2018) Diagnosis and management of spinal muscular atrophy: part 1: recommendations for diagnosis, rehabilitation, orthopedic and nutritional care. Neuromuscul Disord 28(2):103–115. https://doi.org/10.1016/j.nmd.2017.11.005
2. Finkel RS et al (2017) Nusinersen versus sham control in infantile-onset spinal muscular atrophy. N Engl J Med 377(18):1723–1732. https://doi.org/10.1056/NEJMoa1702752
3. Mercuri E et al (2018) Nusinersen versus sham control in later-onset spinal muscular atrophy. N Engl J Med 378(7):625–635. https://doi.org/10.1056/NEJMoa1710504
4. Hagenacker T et al (2020) Nusinersen in adults with 5q spinal muscular atrophy: a non-interventional, multicentre, observational cohort study. Lancet Neurol 19(4):317–325. https://doi.org/10.1016/S1474-4422(20)30037-5
5. SMArtCARE Study Group et al (2023) Improvements in walking distance during nusinersen treatment – a prospective 3-year SMArtCARE Registry Study. J Neuromuscul Dis 10(1):29–40. https://doi.org/10.3233/JND-221600
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1. Improvement in functional motor scores in patients with non-ambulatory spinal muscle atrophy during Nusinersen treatment in South Korea: a single center study;BMC Neurology;2024-06-20
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