Genetic neuromuscular disorders: living the era of a therapeutic revolution. Part 1: peripheral neuropathies-Reference-Cited by-同舟云学术

Genetic neuromuscular disorders: living the era of a therapeutic revolution. Part 1: peripheral neuropathies

Published:2019-03-01 Issue:4 Volume:40 Page:661-669
ISSN:1590-1874
Container-title:Neurological Sciences
language:en
Short-container-title:Neurol Sci

Author:

Vita Giuseppe^ORCID,Vita Gian Luca,Stancanelli Claudia,Gentile Luca,Russo Massimo,Mazzeo Anna

Publisher

Springer Science and Business Media LLC

Subject

Psychiatry and Mental health,Neurology (clinical),Dermatology,General Medicine

Link

http://link.springer.com/content/pdf/10.1007/s10072-019-03778-7.pdf

Reference77 articles.

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2. Hoffman EP, Brown RH Jr, Kunkel LM (1987) Dystrophin: the protein product of the Duchenne muscular dystrophy locus. Cell 51:919–928

3. Ervasti JM, Campbell KP (1993) Dystrophin-associated glycoproteins: their possible roles in the pathogenesis of Duchenne muscular dystrophy. Mol Cell Biol Hum Dis Ser 3:139–166

4. Cossu G, Sampaolesi M (2004) New therapies for muscular dystrophy: cautious optimism. Trends Mol Med 10:516–520

5. Asbury CH (1991) The orphan drug act. The first 7 years. JAMA 265:893–897

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