Preferences of Patients with Amyotrophic Lateral Sclerosis for Intrathecal Drug Delivery: Choosing between an Implanted Drug-Delivery Device and Therapeutic Lumbar Puncture-Reference-Cited by-同舟云学术

Preferences of Patients with Amyotrophic Lateral Sclerosis for Intrathecal Drug Delivery: Choosing between an Implanted Drug-Delivery Device and Therapeutic Lumbar Puncture

Published:2023-12-14 Issue: Volume: Page:
ISSN:1178-1653
Container-title:The Patient - Patient-Centered Outcomes Research
language:en
Short-container-title:Patient

Author:

Seo Jaein,Saurkar Sandeep,Fernandez Gabriela S.,Das Anup,Goutman Stephen A.,Heidenreich Sebastian^ORCID

Funder

Biogen

Publisher

Springer Science and Business Media LLC

Subject

General Engineering

Link

https://link.springer.com/content/pdf/10.1007/s40271-023-00665-4.pdf

Reference86 articles.

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2. Goutman SA, Hardiman O, Al-Chalabi A, Chio A, Savelieff MG, Kiernan MC, Feldman EL. Recent advances in the diagnosis and prognosis of amyotrophic lateral sclerosis. Lancet Neurol. 2022;21:480–93. https://doi.org/10.1016/S1474-4422(21)00465-8.

3. Goutman SA, Hardiman O, Al-Chalabi A, Chio A, Savelieff MG, Kiernan MC, Feldman EL. Emerging insights into the complex genetics and pathophysiology of amyotrophic lateral sclerosis. Lancet Neurol. 2022;21:465–79. https://doi.org/10.1016/S1474-4422(21)00414-2.

4. Lejman J, Panuciak K, Nowicka E, Mastalerczyk A, Wojciechowska K, Lejman M. Gene therapy in ALS and SMA: advances, challenges and perspectives. Int J Mol Sci. 2023;24(2):1130. https://doi.org/10.3390/ijms24021130.

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