Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy-Reference-Cited by-同舟云学术

Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy

Published:2023-07-31 Issue:5 Volume:12 Page:1759-1775
ISSN:2193-8253
Container-title:Neurology and Therapy
language:en
Short-container-title:Neurol Ther

Author:

Obici Laura^ORCID,Ajroud-Driss Senda,Lin Kon-Ping,Berk John L.,Gillmore Julian D.,Kale Parag,Koike Haruki,Danese David,Aldinc Emre,Chen Chongshu,Vest John,Adams David,Wixner Jonas,Backlund Rolf,Pilebro Björn,Anan Intissar,Edbom Fredrik,Ekman Anna,Arvidsson Sandra,Englund Ulrika,Söderberg Karin,Nordh Erik,Uneus Erica,Samuelsson Kristin,Nilzen Anna,Press Rayomand,Bilecen Mirjam,Coelho Teresa,Novais Marta,Rodrigues Patricia,Martins da Silva Ana,Cardoso Inês,Rodrigues Carla,Ramalho Joana,Martins Helder,Silva Mónica,Guimaraes Nádia,Perez Javier,Reis Antonio Hipólito,Monte Julia,Ferreira Natalia,Alves Cristina,Cardoso Marcio,Teixeira Ricardo,Conceição Isabel,Lamas Filipa,Oliveira Santos Miguel,Campos Catarina,de Azevedo Coutinho Conceiçao,Castro José,Castro Isabel,Silva Daniela,Gonçalves Susana,Di Buduo Eleonora,Sforzini Claudia,Mussinelli Roberta,Rosti Vittorio,Lozza Alessandro,Racchi Anna,Sabatelli Mario,Luigetti Marco,Bisogni Giulia,Romano Angela,Guglielmino Valeria,Di Paolantonio Andrea,Bernardo Daniela,Vita Giuseppe,Mazzeo Anna,Russo Massimo,Pareyson Davide,Calabrese Daniela,Fenu Silvia,Saveri Paola,Nienhuis Hans,Bokhorst Geert,Roos Carlien,Couperus Margriet,De Jong Greetje,Brunger Anne,Drost Gea,Lange Fiete,Colauto Adinda,Waddington-Cruz Márcia,Abreu Aline,Pedrosa Roberto Coury,Gervais de Santa Rosa Renata,Dias Moisés,Rakotondratafika Fetra,Echaniz-Laguna Andoni,Cauquil Cecile,Labeyrie Céline,Beaudonnet Guillemette,Boubrit Yasmine,Gaouar Amina,Bourenane Halima,Attarian Shahram,Yahia El Khansa,Verschueren Annie,Grapperon Aude-Marie,Delmont Emilien,Planté-Bordeneuve Violaine,Vervoitte Laetitia,Ayache Samar S.,Le Corvoisier Philippe,Arrouasse Raphaele,Gendre Thierry,Abou Chakra Laure,Focsénéanu Cécile,Barau Caroline,Sole Guilhem,Belin Laurie,Violleau Marie Helene,Duval-Bontemps Fanny,Massie Rami,Dong Xin,Muñoz-Beamud Francisco,García Garrido Sandra,Borrachero Cristina,Gragera Martinez Alvaro,Galán Dávila Lucía,Palacios Marta,Vicente Laura M.,Perez de Isla Leopoldo,Casasnovas Carlos,Díez López Carles,Fabra Elena,González-Costello José,Guerrero Sonia,Yun Viladomat Sergi,Martinez Yurema,Velez-Santamaria Valentina,Nedkova-Hristova Velina,Garcia Pavia Pablo,Gonzalez Segovia Ariadna,De Frutos Fernando,Gonzalez-Lopez Esther,Dominguez Fernando,Escobar-López Luis E.,Cabrera-Romero Eva,Sánchez Gismera Paula,de la Iglesia María,Martinez Valle Fernando,Mazuela Aguila Gonzalo,Lorite Karen,Raguer Núria,Suñé Pilar,Piera Pablo,Ortega Carlos,Aguilar Carla,Gili Gisela,Schmidt Hartmut,Langenstroer Christel,Hüsing-Kabar Anna,Kabar Iyad,Schilling Matthias,Friebel Frauke,Tepasse Phil-Robin,Birklein Frank,Firros Monika,Escolano-Lozano Fabiola,Brueckner Caitlin,Bahnam Vanessa,Kaku Michelle C.,Lau K. H. Vincent,Wiesman Janice,Grogan Martha,Miller Susanna,Frantz Janell,Schmidt Diane C.,AbouEzzeddine Omar,Miller Wayne,Lin Grace,Gertz Morie,Dispenzieri Angela,Brannagan Thomas,Fayerman Raisy,DuVerger Elizabeth,Cabrera Jorge,Maurer Mathew S.,Ulane Christina M.,Weimer Louis H.,Tsang Stephen,Shije Jeffrey,Carberry Nathan,Thu Sai Si,Quan Dianna,Blume Brianna,Overcash J. Scott,Pu He,Lee Kia,Chu Hanh,Zepeda Karla,Waters Michael,Vuong Thao,Coskun Derya,Quillin Kimberly,Davis Allison,Polydefkis Michael,Ye Jing,Li Xiaoling,Khoshnoodi Mohammad,Vista Geno,Chung Tae Hwan,Watt Michele,Tsottles Dan,Masri Ahmad,Carlson Dayna,Drachman Brian,Divito Patricia,Mathelier Hansie,Shanks Margaret,Maslowski Karen,Khella Sami,Pieretti Janice,Joslin Benjamin,Schmidt Emma,Freimer Miriam,Agriesti Julie,Barroso Fabio,Picone Florencia,Lautre Andrea,Orellana Lucas,Du Wenqin,Felius Joost,González-Duarte Alejandra,Cardenas Soto Karla,Traub Rebecca,Chopra Manisha,Chao Chi-Chao,Hsu Chia-Hua,Tsai Li-Kai,Lee Ming-Jen,Su Jen-Jen,Hsieh Sung-Tsang,Hsueh Hsueh-Wen,Chou Hsi-Chieh,Kim Byoung-Joon,Kang Hyesun,Min Ju-Hong,Jeon Eun-Seok,Chung Yeon Hak,Park Jae Hong,Oh Jeeyoung,Jeong Hyun Joo,Tournev Ivailo,Zhelyazkova Sashka,Misumi Yohei,Sakamoto Yumiko,Hashimoto Nami,Misumi Yoshimi,Takahashi Aya,Ueda Mitsuharu,Masuda Teruaki,Ueda Akihiko,Katsuno Masahisa,Tajima Kazuki,Sumi Momoko,Hasegawa Fujiko,Okumura Takahiro,Iijima Masahiro,Fukami Yuki,Ito Daisuke,Kishimoto Yoshiyuki,Kazuta Tomoyuki,Kato Katsuhiko,Mouri Naohiro,Furukawa Soma,Nishi Ryoji,Sekijima Yoshiki,Ito Keiko,Kato Nagaaki,Kishida Dai,Mochizuki Hideki,Okada Kaori,Ohashi Kurumi,Ikenaka Kensuke,Nakamori Masayuki,Kinoshita Makoto,Mapalo Bella Ruth,Law Steven,Chacko Liza,Lachmann Helen,Cohen Oliver,Razvi Yousuf Siu Kay,Varughese Sindhu,Martinez-Naharro Ana,Orrell Richard,Fontana Marianna,Rannigan Lisa,Louth Sarah,Zamba-Papanicolaou Eleni,Charalamnibous Demetra,Manneh Rana Abu,Kleopa Kleopas,Christodoulides Theodoros,Frangos Savvas,Galganski-Cleanthous Michele,Gaglia Eftychia,Smoleski Irene,Kkolou Elena,Ploutarchou Andry,Hanghiuc Mariana,Chroidou Galini,Stylianou Olga,Krokou Anastasia,Zannetou Irene,Kastritis Efstathios,Papadopoulou Dimitra,Spinasas Ilias,Bakalis Panayiotis,Kanellias Nikolaos,Fotiou Despoina,Dialoupi Ioanna,Migko Magdalini,Gavriatopoulou Maria,Low Soon-Chai,Taylor Mark,Stewart Graeme,Knight Helen,Vucic Steve,Carroll Antonia,Silsby Matthew,Suan Dan,Gibbs Simon,Corfield Carmela,Jakicic Suzana,Jina Hayden,Ting Stephen,Wong Shi Qin,Mollee Peter,McKinley Lynda,Abro Emad,Korczyk Dariusz,Remiche Gauthier,Alaerts Nick,De Veylder Fabienne,Claeys Kristl,Debien Elisa,Cremers Joyce,D’hondt Ann,De Wel Bram,

Funder

Alnylam Pharmaceuticals

Publisher

Springer Science and Business Media LLC

Subject

Neurology (clinical),Neurology

Link

https://link.springer.com/content/pdf/10.1007/s40120-023-00522-4.pdf

Reference45 articles.

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