Efficacy and Safety of Valproic Acid for Spinal Muscular Atrophy: A Systematic Review and Meta-Analysis-Reference-Cited by-同舟云学术

Efficacy and Safety of Valproic Acid for Spinal Muscular Atrophy: A Systematic Review and Meta-Analysis

Published:2019-02-22 Issue:3 Volume:33 Page:239-250
ISSN:1172-7047
Container-title:CNS Drugs
language:en
Short-container-title:CNS Drugs

Author:

Elshafay Abdelrahman^ORCID,Hieu Truong Hong^ORCID,Doheim Mohamed Fahmy^ORCID,Kassem Mahmoud Attia Mohamed,ELdoadoa Mohammed Fathi,Holloway Sarah Keturah,Abo-elghar Heba,Hirayama Kenji^ORCID,Huy Nguyen Tien^ORCID

Publisher

Springer Science and Business Media LLC

Subject

Pharmacology (medical),Psychiatry and Mental health,Clinical Neurology

Link

http://link.springer.com/article/10.1007/s40263-019-00606-6/fulltext.html

Reference53 articles.

1. Tizzano EF, Zafeiriou D. Prenatal aspects in spinal muscular atrophy: from early detection to early presymptomatic intervention. Eur J Paediatr Neurol 2018;22(6):944–50.

2. Govoni A, et al. Time is motor neuron: therapeutic window and its correlation with pathogenetic mechanisms in spinal muscular atrophy. Mol Neurobiol. 2018;55(8):6307–18.

3. Verhaart IEC, et al. Prevalence, incidence and carrier frequency of 5q-linked spinal muscular atrophy—a literature review. Orphanet J Rare Dis. 2017;12(1):124.

4. Mostacciuolo ML, et al. Epidemiology of spinal muscular atrophies in a sample of the Italian population. Neuroepidemiology. 1992;11(1):34–8.

5. Wirth B. An update of the mutation spectrum of the survival motor neuron gene (SMN1) in autosomal recessive spinal muscular atrophy (SMA). Hum Mutat. 2000;15(3):228–37.

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