In search of proof-of-concept: gene therapy for glycogen storage disease type Ia
Author:
Publisher
Wiley
Subject
Genetics (clinical),Genetics
Link
http://www.springerlink.com/index/pdf/10.1007/s10545-012-9454-5
Reference59 articles.
1. Alexander IE, Russell DW, Miller AD (1994) DNA-damaging agents greatly increase the transduction of nondividing cells by adeno-associated virus vectors. J Virol 68:8282–8287
2. Baker L, Dahlem S, Goldfarb S et al (1989) Hyperfiltration and renal disease in glycogen storage disease, type I. Kidney Int 35:1345–1350
3. Beaty RM, Jackson M, Peterson D et al (2002) Delivery of glucose-6-phosphatase in a canine model for glycogen storage disease, type Ia, with adeno-associated virus (AAV) vectors. Gene Ther 9:1015–1022
4. Brix AE, Howerth EW, McConkie-Rosell A et al (1995) Glycogen storage disease type Ia in two littermate Maltese puppies. Vet Pathol 32:460–465
5. Chen SJ, Rader DJ, Tazelaar J et al (2000) Prolonged correction of hyperlipidemia in mice with familial hypercholesterolemia using an adeno-associated viral vector expressing very-low-density lipoprotein receptor. Mol Ther 2:256–261
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1. Impaired Glucose Metabolism, Primary Cilium Defects, and Kidney Cystogenesis in Glycogen Storage Disease Type Ia;Journal of the American Society of Nephrology;2024-08-14
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3. Metabolic Diseases of the Liver;Yamada' s Textbook of Gastroenterology;2015-11-27
4. Adeno-Associated Virus Vector–Based Gene Therapy for Monogenetic Metabolic Diseases of the Liver;Journal of Pediatric Gastroenterology & Nutrition;2015-04
5. Hepatic lentiviral gene transfer prevents the long-term onset of hepatic tumours of glycogen storage disease type 1a in mice;Human Molecular Genetics;2015-01-05
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