Exploring the Content Validity of the Unified Wilson Disease Rating Scale: Insights from Qualitative Research
Author:
Funder
Alexion Pharmaceuticals
Publisher
Springer Science and Business Media LLC
Link
https://link.springer.com/content/pdf/10.1007/s12325-024-02833-w.pdf
Reference11 articles.
1. Czlonkowska A, Litwin T, Dusek P, et al. Nature reviews disease primers article: Wilson disease. Nat Rev Dis Primers. 2018;4(1):21. https://doi.org/10.1038/s41572-018-0018-3.
2. Członkowska A, Tarnacka B, Möller JC, et al. Unified Wilson‘s disease rating scale - a proposal for the neurological scoring of Wilson’s disease patients. Neurol Neurochir Pol. 2007;41(1):1–12.
3. Leinweber B, Möller JC, Scherag A, et al. Evaluation of the unified Wilson’s disease rating scale (UWDRS) in German patients with treated Wilson’s disease. Mov Disord. 2008;23(1):54–62. https://doi.org/10.1002/mds.21761.
4. Volpert HM, Pfeiffenberger J, Gröner JB, et al. Comparative assessment of clinical rating scales in Wilson’s disease. BMC Neurol. 2017;17(1):140. https://doi.org/10.1186/s12883-017-0921-3.
5. Patrick DL, Burke LB, Gwaltney CJ, et al. Content validity–establishing and reporting the evidence in newly developed patient-reported outcomes (PRO) instruments for medical product evaluation: ISPOR PRO good research practices task force report: part 1–eliciting concepts for a new PRO instrument. Value Health. 2011;14(8):967–77. https://doi.org/10.1016/j.jval.2011.06.014.
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1. Decoding Wilson disease: a machine learning approach to predict neurological symptoms;Frontiers in Neurology;2024-06-19
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