Safety and Efficacy of Pegcetacoplan in Adult Patients with Paroxysmal Nocturnal Hemoglobinuria over 48 Weeks: 307 Open-Label Extension Study-Reference-Cited by-同舟云学术

Safety and Efficacy of Pegcetacoplan in Adult Patients with Paroxysmal Nocturnal Hemoglobinuria over 48 Weeks: 307 Open-Label Extension Study

Published:2024-04-04 Issue:5 Volume:41 Page:2050-2069
ISSN:0741-238X
Container-title:Advances in Therapy
language:en
Short-container-title:Adv Ther

Author:

Patriquin Christopher J.,Bogdanovic Andrija,Griffin Morag,Kelly Richard J.,Maciejewski Jaroslaw P.,Mulherin Brian,Peffault de Latour Régis,Röth Alexander,Selvaratnam Veena,Szer Jeffrey,Al-Adhami Mohammed,Horneff Regina,Tan Lisa,Yeh Michael,Panse Jens

Funder

Apellis Pharmaceuticals

Swedish Orphan Biovitrum

Publisher

Springer Science and Business Media LLC

Link

https://link.springer.com/content/pdf/10.1007/s12325-024-02827-8.pdf

Reference42 articles.

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2. Brodsky RA. How I treat paroxysmal nocturnal hemoglobinuria. Blood. 2021;137:1304–9. https://doi.org/10.1182/blood.2019003812.

3. Brodsky RA. Paroxysmal nocturnal hemoglobinuria. Blood. 2014;124:2804–11. https://doi.org/10.1182/blood-2014-02-522128.

4. Hill A, Kelly RJ, Hillmen P. Thrombosis in paroxysmal nocturnal hemoglobinuria. Blood. 2013;121:4985–5105. https://doi.org/10.1182/blood-2012-09-311381.

5. Hillmen P, Hall C, Marsh JC, et al. Effect of eculizumab on hemolysis and transfusion requirements in patients with paroxysmal nocturnal hemoglobinuria. N Engl J Med. 2004;350:552–9. https://doi.org/10.1056/NEJMoa031688.

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1. Three Years On: The Role of Pegcetacoplan in Paroxysmal Nocturnal Hemoglobinuria (PNH) since Its Initial Approval;International Journal of Molecular Sciences;2024-08-09