Author:
Hubert Dominique,Marguet Christophe,Benichou Jacques,DeSouza Cynthia,Payen-Champenois Catherine,Kinnman Nils,Chandarana Keval,Munck Anne,Fajac Isabelle,Ramel Sophie,Vigneron Philippe,Storni Veronique,Remus Natacha,Durieu Laurence Bassinet Isabelle,Laurans Muriel,Troussier Cinthia Rames Françoise,Huet Marie-Laure Dalphin Frédéric,Pin Isabelle,Payet Boubou Camara Annabelle,Languepin Jeanne,Danner-Boucher Isabelle,Mankikian Marc Albertini Julie,Wizla Nathalie,Cosson Laure,Mittaine Eric Deneuville Marie,Reix Philippe,Dufeu Nadine,David Valérie,Bui Thierry Langin Stéphanie,Chiron Raphael,Grenet Dominique,Chedevergne Frédérique,Belleguic Chantal,Mely Laurent,
Publisher
Springer Science and Business Media LLC
Subject
Pulmonary and Respiratory Medicine,Respiratory Care
Reference29 articles.
1. Van Goor F, Hadida S, Grootenhuis PD, Burton B, Cao D, Neuberger T, et al. Rescue of CF airway epithelial cell function in vitro by a CFTR potentiator, VX-770. Proc Natl Acad Sci USA. 2009;106(44):18825–30. https://doi.org/10.1073/pnas.0904709106.
2. Van Goor F, Yu H, Burton B, Hoffman BJ. Effect of ivacaftor on CFTR forms with missense mutations associated with defects in protein processing or function. J Cyst Fibros. 2014;13(1):29–36. https://doi.org/10.1016/j.jcf.2013.06.008.
3. Yu H, Burton B, Huang CJ, Worley J, Cao D, Johnson JP Jr, et al. Ivacaftor potentiation of multiple CFTR channels with gating mutations. J Cyst Fibros. 2012;11(3):237–45. https://doi.org/10.1016/j.jcf.2011.12.005.
4. European Medicines Agency. Summary of opinion (initial authorisation). https://www.ema.europa.eu/en/documents/smop-initial/chmp-summary-positive-opinion-kalydeco_en.pdf (2012). Accessed Oct 5, 2020.
5. Haute Autorité de Santé. Transparency committee: opinion. https://www.has-sante.fr/upload/docs/application/pdf/2013-05/kalydeco_ct_12474.pdf. Accessed Oct 5, 2020.
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