Use of Tricyclo-DNA Antisense Oligonucleotides for Exon Skipping
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Publisher
Springer New York
Link
http://link.springer.com/content/pdf/10.1007/978-1-4939-8651-4_24
Reference15 articles.
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3. Relizani K, Griffith G, Echevarría L et al (2017) Efficacy and safety profile of Tricyclo-DNA antisense oligonucleotides in Duchenne muscular dystrophy mouse model. Mol Ther Nucleic Acids 8:144–157
4. Robin V, Griffith G, Carter J-PL et al (2017) Efficient SMN rescue following subcutaneous Tricyclo-DNA antisense oligonucleotide treatment. Mol Ther Nucleic Acids 7:81–89
5. McClorey G, Wood MJ (2015) An overview of the clinical application of antisense oligonucleotides for RNA-targeting therapies. Curr Opin Pharmacol 24:52–58
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