A combined approach for β-thalassemia based on gene therapy-mediated adult hemoglobin (HbA) production and fetal hemoglobin (HbF) induction-Reference-Cited by-同舟云学术

A combined approach for β-thalassemia based on gene therapy-mediated adult hemoglobin (HbA) production and fetal hemoglobin (HbF) induction

Published:2012-03-31 Issue:8 Volume:91 Page:1201-1213
ISSN:0939-5555
Container-title:Annals of Hematology
language:en
Short-container-title:Ann Hematol

Author:

Zuccato Cristina,Breda Laura,Salvatori Francesca,Breveglieri Giulia,Gardenghi Sara,Bianchi Nicoletta,Brognara Eleonora,Lampronti Ilaria,Borgatti Monica,Rivella Stefano,Gambari Roberto

Publisher

Springer Science and Business Media LLC

Subject

Hematology,General Medicine

Link

http://www.springerlink.com/index/pdf/10.1007/s00277-012-1430-5

Reference58 articles.

1. Steinberg MH, Forget BG, Higgs DR, Nagel RL (2001) Disorders of hemoglobin: genetics, pathophysiology and clinical management. Cambridge University Press, Cambridge, UK

2. Thein SL (2004) Genetic insights into the clinical diversity of beta thalassaemia. Br J Haematol 124:264–274

3. Old JM (2003) Screening and genetic diagnosis of haemoglobin disorders. Blood Rev 17:43–53

4. Bank A (2006) Regulation of human fetal hemoglobin: new players, new complexities. Blood 107:435–443

5. Stamatoyannopoulos G (2005) Control of globin gene expression during development and erythroid differentiation. Exp Hematol 33:259–271

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