Variation of tafamidis plasma levels during the treatment of TTR amyloidosis patients with Glu89Gln mutation
Author:
Publisher
Springer Science and Business Media LLC
Subject
Pharmacology (medical),Pharmacology,General Medicine
Link
https://link.springer.com/content/pdf/10.1007/s00228-023-03576-3.pdf
Reference20 articles.
1. Müller ML, Butler J, Heidecker B (2020) Emerging therapies in transthyretin amyloidosis – a new wave of hope after years of stagnancy? Eur J Heart Fail 22(1):39–53
2. Burton A, Castaño A, Bruno M et al (2021) Drug discovery and development in rare diseases: taking a closer look at the tafamidis story. Drug Des Devel Ther 15:1225–1243
3. Mundayat R, Stewart M, Alvir J et al (2018) Positive effectiveness of tafamidis in delaying disease progression in transthyretin familial amyloid polyneuropathy up to 2 years: an analysis from the transthyretin amyloidosis outcomes survey (THAOS). Neurol Ther 7(1):87–101
4. Ando Y, Coelho T, Berk JL et al (2013) Guideline of transthyretin-related hereditary amyloidosis for clinicians. Orphanet J Rare Dis 8(1):1–18
5. Park J, Egolum U, Parker S et al (2020) Tafamidis: a first-in-class transthyretin stabilizer for transthyretin amyloid cardiomyopathy. Ann Pharmacother 54(5):470–477
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