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https://rarediseases.info.nih.gov/diseases/pages/31/faqs-about-rare-diseases
. Accessed 31 Oct 2018
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https://www.fda.gov/ForIndustry/DevelopingProductsforRareDiseasesConditions/HowtoapplyforOrphanProductDesignation/ucm364750.htm
. Accessed 31 Oct 2018
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https://www.fda.gov/downloads/forindustry/developingproductsforrarediseasesconditions/ucm351283.pdf
. Accessed 31 Oct 2018
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https://www.fda.gov/downloads/RegulatoryInformation/Guidances/UCM589710.pdf
. Accessed 12 Apr 2018
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