Equity, Access and Economic Evaluation in Rare Diseases

Author:

Bosanquet Nick,Domenighetti Gianfranco,Beresniak Ariel,Auray Jean-Paul,Crivelli Luca,Richard Lance,Howard Paul

Publisher

Springer Science and Business Media LLC

Subject

Anesthesiology and Pain Medicine

Reference37 articles.

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2. Haffner ME. Orphan products: origins, progress, and prospects. Annu Rev Pharmacol Toxicol 1991; 31: 603–20

3. Haffner ME, Kelsey JV. Evaluation of orphan products by the US Food and Drug Administration. Int J Technol Assess Health Care 1992; 8: 647–57

4. US Food and Drug Administration. How to apply for designation as an orphan product [online]. Available from URL: http://www.fda.gov/orphan/designat/apply.htm [Accessed 2003 May 1]

5. Myers AS. Orphan drugs: the current situation in the United States, Europe, and Asia. Drug Inf J 1997; 31: 101–4

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