Gene Therapies for Polyglutamine Diseases-Reference-Cited by-同舟云学术

Gene Therapies for Polyglutamine Diseases

Published:2018 Issue: Volume: Page:395-438
ISSN:0065-2598
Container-title:Polyglutamine Disorders
language:
Short-container-title:

Author:

Matos Carlos A.,Carmona Vítor,Vijayakumar Udaya-Geetha,Lopes Sara,Albuquerque Patrícia,Conceição Mariana,Nobre Rui Jorge,Nóbrega Clévio,de Almeida Luís Pereira

Publisher

Springer International Publishing

Link

http://link.springer.com/content/pdf/10.1007/978-3-319-71779-1_20

Reference287 articles.

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3. Gatchel JR, Zoghbi HY (2005) Diseases of unstable repeat expansion: mechanisms and common principles. Nat Rev Genet 6:743–755

4. Hsu PD, Lander ES, Zhang F (2014) Development and applications of CRISPR-Cas9 for genome engineering. Cell 157:1262–1278

5. Boudreau RL, Rodriguez-Lebron E, Davidson BL (2011) RNAi medicine for the brain: progresses and challenges. Hum Mol Genet 20:R21–R27

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