Modified Antisense Oligonucleotides and Their Analogs in Therapy of Neuromuscular Diseases
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Publisher
Springer International Publishing
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http://link.springer.com/content/pdf/10.1007/978-3-319-34175-0_11
Reference141 articles.
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3. Alter J, Lou F, Rabinowitz A et al (2006) Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology. Nat Med 12:175
4. Aoki Y, Yokota T, Nagata T et al (2012) Bodywide skipping of exons 45–55 in dystrophic mdx52 mice by systemic antisense delivery. Proc Natl Acad Sci USA 109:13763–13768
5. Ashizawa T, Harper PS (2006) Myotonic dystrophies: an overview. In: Ashizawa T, Wells RD (eds) Genetic instabilities and neurological disorders, 2nd edn. Elsevier, Burlington, pp 21–36
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