Evolving Therapeutic Options for the Treatment of Duchenne Muscular Dystrophy
Author:
Publisher
Elsevier BV
Subject
Pharmacology (medical),Neurology (clinical),Pharmacology
Link
https://link.springer.com/content/pdf/10.1007/s13311-023-01423-y.pdf
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3. Glucocorticoid corticosteroids for Duchenne muscular dystrophy;Manzur;Cochrane Database Syst Rev.,2008
4. Clinical investigation of Duchenne muscular dystrophy. A methodology for therapeutic trials based on natural history controls;Mendell;Arch Neurol.,1987
5. Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study;McDonald;Lancet Lond Engl,2018
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