In Vivo Administration of Splice Switching PNAs Using the mdx Mouse as a Model System-Reference-Cited by-同舟云学术

In Vivo Administration of Splice Switching PNAs Using the mdx Mouse as a Model System

Published:2020 Issue: Volume: Page:241-250
ISSN:1064-3745
Container-title:Peptide Nucleic Acids
language:
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Author:

Brolin Camilla,Lim Ernest Wee Kiat,Nielsen Peter E.

Publisher

Springer US

Link

http://link.springer.com/content/pdf/10.1007/978-1-0716-0243-0_15

Reference15 articles.

1. Yin H, Lu Q, Wood M (2008) Effective exon skipping and restoration of dystrophin expression by peptide nucleic acid antisense oligonucleotides in mdx mice. Mol Ther 16(1):38–45. https://doi.org/10.1038/sj.mt.6300329

2. Yin H, Betts C, Saleh AF, Ivanova GD, Lee H, Seow Y, Kim D, Gait MJ, Wood MJ (2010) Optimization of peptide nucleic acid antisense oligonucleotides for local and systemic dystrophin splice correction in the mdx mouse. Mol Ther 18(4):819–827. https://doi.org/10.1038/mt.2009.310

3. Ivanova GD, Arzumanov A, Abes R, Yin H, Wood MJ, Lebleu B, Gait MJ (2008) Improved cell-penetrating peptide-PNA conjugates for splicing redirection in HeLa cells and exon skipping in mdx mouse muscle. Nucleic Acids Res 36(20):6418–6428. https://doi.org/10.1093/nar/gkn671

4. Willmann R, Possekel S, Dubach-Powell J, Meier T, Ruegg MA (2009) Mammalian animal models for Duchenne muscular dystrophy. Neuromuscul Disord 19(4):241–249

5. TREAT-NMD Neuromuscular Network (2018, June 14) Experimental protocols for DMD animal models. http://www.treat-nmd.eu/research/preclinical/dmd-sops/

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