Engaging patients and caregivers in prioritizing symptoms impacting quality of life for Duchenne and Becker muscular dystrophy
Author:
Funder
Parent Project Muscular Dystrophy
Publisher
Springer Science and Business Media LLC
Subject
Public Health, Environmental and Occupational Health
Link
https://link.springer.com/content/pdf/10.1007/s11136-018-1891-7.pdf
Reference47 articles.
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2. Emery, A. E. (1991). Population frequencies of inherited neuromuscular diseases: A world survey. Neuromuscular Disorders, 1(1), 19–29.
3. Mah, J. K., Korngut, L., Dykeman, J., Day, L., Pringsheim, T., & Jette, N. (2014). A systematic review and meta-analysis on the epidemiology of Duchenne and Becker muscular dystrophy. Neuromuscular Disorders, 24(6), 482–491.
4. Bushby, K., Finkel, R., Birnkrant, D. J., Case, L. E., Clemens, P. R., Cripe, L., et al. (2010). Diagnosis and management of Duchenne muscular dystrophy, part 1: Diagnosis, and pharmacological and psychosocial management. The Lancet. Neurology, 9(1), 77–93.
5. Cyrulnik, S. E., Fee, R. J., Batchelder, A., Kiefel, J., Goldstein, E., & Hinton, V. J. (2008). Cognitive and adaptive deficits in young children with Duchenne muscular dystrophy (DMD). Journal of the International Neuropsychological Society, 14(5), 853–861.
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