Overview on DMD Exon Skipping
Author:
Publisher
Humana Press
Link
http://link.springer.com/content/pdf/10.1007/978-1-61779-767-5_7.pdf
Reference85 articles.
1. Aartsma-Rus A, van Ommen GJ (2007) Antisense-mediated exon skipping: a versatile tool with therapeutic and research applications. RNA 13:1609–1624
2. van Ommen GJ, van Deutekom J, Aartsma-Rus A (2008) The therapeutic potential of antisense-mediated exon skipping. Curr Opin Mol Ther 10:140–149
3. Aartsma-Rus A (2010) Antisense-mediated modulation of splicing: therapeutic implications for duchenne muscular dystrophy. RNA Biol 7(4):453–461
4. Emery AE (2002) The muscular dystrophies. Lancet 359:687–695
5. Hoffman EP, Brown RH Jr, Kunkel LM (1987) Dystrophin: the protein product of the Duchenne muscular dystrophy locus. Cell 51:919–928
Cited by 41 articles. 订阅此论文施引文献 订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献
1. Possibilities and limitations of antisense oligonucleotide therapies for the treatment of monogenic disorders;Communications Medicine;2024-01-05
2. Antisense Oligonucleotide-Mediated Splice Switching: Potential Therapeutic Approach for Cancer Mitigation;Cancers;2021-11-05
3. ActRIIB:ALK4-Fc alleviates muscle dysfunction and comorbidities in murine models of neuromuscular disorders;Journal of Clinical Investigation;2021-02-15
4. Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy;JAMA Neurology;2020-09-01
5. Limb-girdle Muscular Dystrophy and Therapy: Insights into Cell and Gene-based Approaches;Current Gene Therapy;2020-04-25
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线，采集、加工和组织学术论文而形成的新型学术文献查询和分析系统，可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容，当前同舟云学术共收录了国内外主流学术期刊6万余种，收集的期刊论文及会议论文总量共计约1.5亿篇，并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询！咨询电话：010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3