AAV-Mediated Gene Therapy to the Isolated Limb in Rhesus Macaques
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Publisher
Humana Press
Link
http://link.springer.com/content/pdf/10.1007/978-1-61737-982-6_19.pdf
Reference7 articles.
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2. Wang, Z., Chamberlain, J. S., Tapscott, S. J., and Storb, R. (2009). Gene therapy in large animal models of muscular dystrophy. ILAR J 50, 187–198.
3. Harper, S. Q., et al. (2002). Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy. Nat Med 8, 253–261.
4. Liu, M., Yue, Y., Harper, S. Q., Grange, R. W., Chamberlain, J. S., and Duan, D. (2005). Adeno-associated virus-mediated microdystrophin expression protects young mdx muscle from contraction-induced injury. Mol Ther 11, 245–256.
5. Rodino-Klapac, L. R., et al. (2007). A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy. J Transl Med 5, 45.
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