Combinatorial Gene Therapy Strategies for Treating Muscular Dystrophies
Author:
Publisher
Springer New York
Link
http://link.springer.com/content/pdf/10.1007/978-1-4419-1207-7_8.pdf
Reference129 articles.
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3. Bartoli, M., Poupiot, J., Vulin, A., Fougerousse, F., Arandel, L., Daniele, N., Roudaut, C., Noulet, F., Garcia, L., Danos, O., et al. (2007). AAV-mediated delivery of a mutated myostatin propeptide ameliorates calpain 3 but not alpha-sarcoglycan deficiency. Gene Ther 14, 733–740.
4. Barton, E.R., Morris, L., Musaro, A., Rosenthal, N., and Sweeney, H.L. (2002). Muscle-specific expression of insulin-like growth factor I counters muscle decline in mdx mice. J Cell Biol 157, 137–148.
5. Barton-Davis, E.R., Shoturma, D.I., Musaro, A., Rosenthal, N., and Sweeney, H.L. (1998). Viral mediated expression of insulin-like growth factor I blocks the aging-related loss of skeletal muscle function. Proc Natl Acad Sci U S A 95, 15603–15607.
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