CRISPR/Cas9, a promising approach for the treatment of β-thalassemia: a systematic review
Author:
Funder
bam university of medical sciences
Publisher
Springer Science and Business Media LLC
Subject
Genetics,Molecular Biology,General Medicine
Link
https://link.springer.com/content/pdf/10.1007/s00438-022-01978-z.pdf
Reference56 articles.
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2. Antoniani C, Meneghini V, Lattanzi A, Felix T, Romano O, Magrin E et al (2018) induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus. Blood 131(17):1960–1973
3. Arumugam P, Malik P (2010). Genetic therapy for beta-thalassemia: from the bench to the bedside. In: Hematology 2010, the American Society of Hematology Education Program Book, 2010(1):445–50
4. Cai L, Bai H, Mahairaki V, Gao Y, He C, Wen Y et al (2018) A Universal approach to correct various HBB gene mutations in human stem cells for gene therapy of beta-Thalassemia and sickle cell disease. Stem Cells Transl Med 7(1):87–97
5. Cao A, Galanello R (2010) Beta-thalassemia. Genet Med 12(2):61–76
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