How to Design a Therapeutic Trial in SCAs
Author:
Publisher
Springer International Publishing
Link
https://link.springer.com/content/pdf/10.1007/978-3-031-24345-5_8
Reference90 articles.
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4. Ashizawa T, Figueroa KP, Perlman SL, et al. Clinical characteristics of patients with spinocerebellar ataxias 1, 2, 3 and 6 in the US; a prospective observational study. Orphanet J Rare Dis. 2013;8:177. https://doi.org/10.1186/1750-1172-8-177.
5. Ashizawa T, Öz G, Paulson HL. Spinocerebellar ataxias: prospects and challenges for therapy development. Nat Rev Neurol. 2018;14:590–605. https://doi.org/10.1038/s41582-018-0051-6.
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