Splice-correcting oligonucleotides restore BTK function in X-linked agammaglobulinemia model-Reference-Cited by-同舟云学术

Splice-correcting oligonucleotides restore BTK function in X-linked agammaglobulinemia model

Published:2014-08-08 Issue:9 Volume:124 Page:4067-4081
ISSN:0021-9738
Container-title:Journal of Clinical Investigation
language:en
Short-container-title:J. Clin. Invest.

Author:

Bestas Burcu,Moreno Pedro M.D.,Blomberg K. Emelie M.,Mohammad Dara K.,Saleh Amer F.,Sutlu Tolga,Nordin Joel Z.,Guterstam Peter,Gustafsson Manuela O.,Kharazi Shabnam,Piątosa Barbara,Roberts Thomas C.,Behlke Mark A.,Wood Matthew J.A.,Gait Michael J.,Lundin Karin E.,El Andaloussi Samir,Månsson Robert,Berglöf Anna,Wengel Jesper,Smith C.I. Edvard

Publisher

American Society for Clinical Investigation

Subject

General Medicine

Reference78 articles.

1. Agammaglobulinemia: causative mutations and their implications for novel therapies

2. Primary B Cell Immunodeficiencies: Comparisons and Contrasts

3. Bruton’s tyrosine kinase (Btk): function, regulation, and transformation with special emphasis on the PH domain

4. The gene involved in X-linked agammaglobulinaemia is a member of the src family of protein-tyrosine kinases

5. Deficient expression of a B cell cytoplasmic tyrosine kinase in human X-linked agammaglobulinemia

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