Phase I/II Study of Intrapleural Administration of a Serotype rh.10 Replication-Deficient Adeno-Associated Virus Gene Transfer Vector Expressing the Human α1-Antitrypsin cDNA to Individuals with α1-Antitrypsin Deficiency-Reference-Cited by-同舟云学术

Phase I/II Study of Intrapleural Administration of a Serotype rh.10 Replication-Deficient Adeno-Associated Virus Gene Transfer Vector Expressing the Human α1-Antitrypsin cDNA to Individuals with α1-Antitrypsin Deficiency

Published:2014-09 Issue:3 Volume:25 Page:112-133
ISSN:2324-8637
Container-title:Human Gene Therapy Clinical Development
language:en
Short-container-title:Human Gene Therapy Clinical Development

Author:

Chiuchiolo Maria J.¹,Kaminsky Stephen M.¹,Sondhi Dolan¹,Mancenido Denesy¹,Hollmann Charleen¹,Crystal Ronald G.¹

Affiliation:

1. Department of Genetic Medicine, Weill Cornell Medical College, New York, NY 10065.

Publisher

Mary Ann Liebert Inc

Subject

Genetics (clinical)

Link

http://www.liebertpub.com/doi/pdf/10.1089/humc.2014.2513

Reference108 articles.

1. Long-term expression of the human α1-antitrypsin gene in mice employing anionic and cationic liposome vector

2. In Vivo Delivery of Human α1-Antitrypsin Gene to Mouse Hepatocytes by Liposomes

3. Expression of Human α1-Antitrypsin in Mouse After in Vivo Gene Transfer to Hepatocytes by Small Liposomes

4. Survival and FEV1Decline in Individuals with Severe Deficiency of α1-Antitrypsin

5. Safety of Direct Laryngoscopy As an Outpatient Procedure

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