Non-Clinical Efficacy and Safety Studies on G1XCGD, a Lentiviral Vector for Ex Vivo Gene Therapy of X-Linked Chronic Granulomatous Disease-Reference-Cited by-同舟云学术

Non-Clinical Efficacy and Safety Studies on G1XCGD, a Lentiviral Vector for Ex Vivo Gene Therapy of X-Linked Chronic Granulomatous Disease

Published:2018-06 Issue:2 Volume:29 Page:69-79
ISSN:2324-8637
Container-title:Human Gene Therapy Clinical Development
language:en
Short-container-title:Human Gene Therapy Clinical Development

Author:

Brendel Christian¹²³⁴⁵,Rothe Michael⁶,Santilli Giorgia⁷,Charrier Sabine⁸,Stein Stefan¹,Kunkel Hana¹,Abriss Daniela¹,Müller-Kuller Uta¹,Gaspar Bobby⁷,Modlich Ute⁶⁹,Galy Anne⁸,Schambach Axel²⁶¹⁰,Thrasher Adrian J.⁷,Grez Manuel¹

Affiliation:

1. Institute for Tumor Biology and Experimental Therapy, Georg-Speyer-Haus, Frankfurt, Germany.

2. Division of Hematology/Oncology, Boston Children's Hospital, Boston, Massachusetts.

3. Harvard Medical School, Boston, Massachusetts.

4. Pediatric Oncology, Dana-Farber Cancer Institute, Boston, Massachusetts.

5. Harvard Stem Cell Institute, Harvard University, Boston, Massachusetts.

6. Hannover Medical School, Institute of Experimental Hematology, Hannover, Germany.

7. UCL Great Ormond Street Institute of Child Health, and Great Ormond Street Hospital for Children NHS Trust London, United Kingdom.

8. Genethon, Evry, France.

9. Research Group Gene Modification in Stem Cells, Paul-Ehrlich-Institute, Langen, Germany.

10. Hannover Medical School, Cluster of Excellence REBIRTH, Hannover, Germany.

Publisher

Mary Ann Liebert Inc

Subject

Genetics (clinical)

Link

http://www.liebertpub.com/doi/pdf/10.1089/humc.2017.245

Reference27 articles.

1. Chronic Granulomatous Disease

2. The Genetic Basis of Chronic Granulomatous Disease

3. The NADPH oxidase and chronic granulomatous disease

4. Chronic Granulomatous Disease: The European Experience

5. Genetic, Biochemical, and Clinical Features of Chronic Granulomatous Disease

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